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PaysNew Zealandlocalisation
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Synchronisé depuis ClinicalTrials.gov — NCT03981575

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Essais cliniques associés

4
MoléculeIndication / populationPhaseNCTTitreStatut
GRASP-01-002 — Defining Endpoints in Becker Muscular Dystrophy Myopathies À vérifier NCT05257473 GRASP-01-002 — Defining Endpoints in Becker Muscular Dystrophy ACTIVE_NOT_RECRUITING
Estab Biomarkers and Clinical Endpoints in Myotonic Dystrophy Type 1 (END-DM1) Myopathies À vérifier NCT03981575 Estab Biomarkers and Clinical Endpoints in Myotonic Dystrophy Type 1 (END-DM1) RECRUITING
zeleciment basivarsen (DYNE-101) Myopathies Phase 3 NCT07486934 Efficacy, Safety, and Tolerability of Zeleciment Basivarsen (DYNE-101) in Participants With Myotonic Dystrophy Type 1 RECRUITING
XEN1101 Épilepsie Phase 3 NCT05718817 X-TOLE4 — An Open-label Study of XEN1101 in Epilepsy ENROLLING_BY_INVITATION