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Boston Children's Hospital
Boston — United States
Essais liés23clinical trials
VilleBostonlocalisation
PaysUnited Stateslocalisation
SourcelocaleCSV/MySQL
Informations
centreSynchronisé depuis ClinicalTrials.gov — NCT05104983
Essais cliniques associés
23| Molécule | Indication / population | Phase | NCT | Titre | Statut |
|---|---|---|---|---|---|
| EXCOR Active Driving System for Pediatric VAD | Insuffisance cardiaque | Non applicable | NCT05610787 | EXCOR Active Driving System for the EXCOR Pediatric VAD IDE Study | ENROLLING_BY_INVITATION |
| Tripolar electroencephalography | Épilepsie | À vérifier | NCT05944692 | Epilepsy Seizure Detection With Innovative Tripolar EEG (tEEG) | RECRUITING |
| delandistrogene moxeparvovec | Myopathies | À vérifier | NCT06270719 | ENDURE — An Observational Study Comparing Delandistrogene Moxeparvovec (ELEVIDYS) With Standard of Care in Participants With Duchenne Muscular Dystrophy | ENROLLING_BY_INVITATION |
| CLN-978 | Lupus | Phase 1 | NCT06613360 | A Study of CLN-978, a Subcutaneously Administered CD19-directed T Cell Engager, in Subjects With Systemic Lupus Erythematosus | RECRUITING |
| Ketogenic diet | Épilepsie | Phase 1 | NCT06700811 | Ketogenic Diet for Prevention of Epileptic Spasms in Infantile Onset Genetic Epilepsies | TERMINATED |
| Sirolimus | Épilepsie | Phase 2 | NCT05104983 | TSC-STEPS — Stopping TSC Onset and Progression 2B: Sirolimus TSC Epilepsy Prevention Study | ACTIVE_NOT_RECRUITING |
| NS-089/NCNP-02 | Myopathies | Phase 2 | NCT05996003 | NS-089/NCNP-02-201 in Boys With Duchenne Muscular Dystrophy (DMD) | ACTIVE_NOT_RECRUITING |
| Outcomes of Neurosurgical Tone Management | Myopathies | À vérifier | NCT07817745 | Outcomes of Neurosurgical Tone Management | RECRUITING |
| Soticlestat | Épilepsie | Phase 2 | NCT03635073 | Endymion 1 — A Study of Soticlestat in Adults and Children With Rare Epilepsies | TERMINATED |
| Observation Study in Patients Age 0-5 Years With LAMA2-related Congenital Muscular Dystrophy | Myopathies | À vérifier | NCT06503367 | Observation Study in Patients Age 0-5 Years With LAMA2-related Congenital Muscular Dystrophy | RECRUITING |
| CABA-201 | Lupus | Phase 1/2 | NCT06121297 | RESET-SLE: A Phase 1/2 Open-Label Study to Evaluate the Safety and Efficacy of CABA-201 in Subjects With Active Systemic Lupus Erythematosus | RECRUITING |
| Anakinra | Épilepsie | Phase 3 | NCT07281027 | COMparison Between Anakinra and Tocilizumab in NORSE - "COMBAT-NORSE" | NOT_YET_RECRUITING |
| Deramiocel (CAP-1002) | Myopathies | Phase 3 | NCT05126758 | HOPE-3 — A Study of Deramiocel (CAP-1002) in Ambulatory and Non-Ambulatory Patients With Duchenne Muscular Dystrophy | ACTIVE_NOT_RECRUITING |
| VX-670 | Myopathies | Phase 1/2 | NCT06185764 | Galileo — A Phase 1/2 Study of VX-670 in Adult Participants With Myotonic Dystrophy 1 (DM1) | ACTIVE_NOT_RECRUITING |
| PROVIDUS — A Study Evaluating the Real-World Experience of Givinostat in Patients With Duchenne Muscular Dystrophy | Myopathies | À vérifier | NCT07127978 | PROVIDUS — A Study Evaluating the Real-World Experience of Givinostat in Patients With Duchenne Muscular Dystrophy | RECRUITING |
| LMY-922 | Lupus | Phase 1 | NCT07729995 | BAFF CAR-T Cells (LMY-922) for Treatment of Refractory Autoimmune Disease | NOT_YET_RECRUITING |
| Online Study of People Who Have Genetic Changes and Features of Autism: Simons Searchlight | Épilepsie | À vérifier | NCT01238250 | Online Study of People Who Have Genetic Changes and Features of Autism: Simons Searchlight | RECRUITING |
| ETX101 | Épilepsie | Phase 1/2 | NCT05419492 | ENDEAVOR — A Clinical Study to Evaluate the Safety and Efficacy of ETX101 in Infants and Children With SCN1A-Positive Dravet Syndrome | RECRUITING |
| ASP2957 | Myopathies | Phase 1/2 | NCT07052929 | Study of ASP2957 in Male Participants With X-linked Myotubular Myopathy Who Need Ventilators | RECRUITING |
| EXCEL — A Study to Check Liver Health in Boys With XLMTM, a Serious Genetic Muscle Condition | Myopathies | À vérifier | NCT06581146 | EXCEL — A Study to Check Liver Health in Boys With XLMTM, a Serious Genetic Muscle Condition | RECRUITING |
| zorevunersen | Épilepsie | Phase 3 | NCT06872125 | A Double-blind Study Evaluating the Efficacy, Safety, and Tolerability of Zorevunersen in Patients With Dravet Syndrome | ACTIVE_NOT_RECRUITING |
| S230815- Starting dose A | Épilepsie | Phase 1/2 | NCT07227857 | KANDLE — A First-in-human Study of S230815 in Pediatric Participants With KCNT1-related Developmental and Epileptic Encephalopathy | RECRUITING |
| Casimersen | Myopathies | Phase 3 | NCT03532542 | An Extension Study to Evaluate Casimersen or Golodirsen in Patients With Duchenne Muscular Dystrophy | TERMINATED |