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Synchronisé depuis ClinicalTrials.gov — NCT04288726

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Essais cliniques associés

9
MoléculeIndication / populationPhaseNCTTitreStatut
Eteplirsen Myopathies À vérifier NCT06606340 EVOLVE — A Long-term Observational Study Evaluating Eteplirsen, Golodirsen, or Casimersen in Routine Clinical Practice ENROLLING_BY_INVITATION
Biospecimen Collection Cancer Phase 1/2 NCT01089101 Selumetinib in Treating Young Patients With Recurrent or Refractory Low Grade Glioma ACTIVE_NOT_RECRUITING
EXCOR Active Driving System for Pediatric VAD Insuffisance cardiaque Non applicable NCT05610787 EXCOR Active Driving System for the EXCOR Pediatric VAD IDE Study ENROLLING_BY_INVITATION
Ataluren Myopathies Phase 3 NCT01247207 Study of Ataluren in Previously Treated Participants With Nonsense Mutation Dystrophinopathy (nmDBMD) TERMINATED
CD30.CAR-EBVST cells Cancer Phase 1 NCT04288726 Allogeneic CD30.CAR-EBVSTs in Patients With Relapsed or Refractory CD30-Positive Lymphomas ACTIVE_NOT_RECRUITING
Obecabtagene autoleucel Lupus Phase 2 NCT07053800 LUMINA — Obe-cel in Severe, Refractory Systemic Lupus Erythematosus (SLE) With Active Lupus Nephritis (LN) RECRUITING
zorevunersen Épilepsie Phase 3 NCT06872125 A Double-blind Study Evaluating the Efficacy, Safety, and Tolerability of Zorevunersen in Patients With Dravet Syndrome ACTIVE_NOT_RECRUITING
Casimersen Myopathies Phase 3 NCT03532542 An Extension Study to Evaluate Casimersen or Golodirsen in Patients With Duchenne Muscular Dystrophy TERMINATED
baclofen Myopathies Phase 1 NCT00607542 Oral Baclofen Pharmacokinetics and Pharmacodynamics in Children With Spasticity COMPLETED