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Périmètre

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Chaque choix s’applique immédiatement aux quatre sections. Le filtre « type de SEP » n’apparaît que lorsque la sclérose en plaques est sélectionnée.

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Essais et traitements4050Données cliniques et programmes
Recherches et trouvailles21Pipeline scientifique
Publications4595Références reliées aux maladies
Pistes exploratoires0Hypothèses non validées
8666 résultats correspondants · 41 visibles sur cette page dans le périmètre Toutes les maladies
Niveau clinique

Études et traitements 4050

Interventions, programmes et essais cliniques rattachés au périmètre sélectionné.

Molécule / élément Maladie / population Objectif Phase / stade Statut / preuve Mécanisme / résumé Source Détail
Laminectomy and bone marrow stem cells transplantation NCT01254539 · Clinical Trial on The Use of Autologous Bone Marrow Stem Cells in Amyotrophic La… Sclérose latérale amyotrophique Thérapie cellulaire Phase 1 COMPLETED Description non affichée : incohérence de maladie détectée. Consultez l’es… À vérifier ClinicalTrials.gov 2026-07-10 00:13:42 Détail
ONO-2506PO NCT00694941 · A Phase II Multi-centre, Extension Study to Investigate the Long Term Safety of… Sclérose latérale amyotrophique À vérifier Phase 2 COMPLETED Description non affichée : incohérence de maladie détectée. Consultez l’es… À vérifier ClinicalTrials.gov 2026-07-10 00:13:42 Détail
Amifampridine Phosphate NCT03304054 · Study to Evaluate Amifampridine Phosphate in Patients With MuSK-MG Myasthénie À vérifier Phase 3 COMPLETED Efficacy and safety of amifampridine phosphate in improving the activities… À vérifier ClinicalTrials.gov 2026-07-10 00:13:41 Détail
HBI0101 CART NCT07085676 · Phase 1 Study of HBI0101 CAR-T in Refractory B-Cell Autoimmune Diseases Myasthénie Thérapie cellulaire Phase 1 RECRUITING A Phase 1 study of HBI0101 BCMA-CART in B-Cell Mediated Autoimmune Rheumat… À vérifier ClinicalTrials.gov 2026-07-10 00:13:41 Détail
HBM9161 Injection (680mg and 340 mg) NCT04346888 · A Study to Evaluate the Efficacy, Safety and PD and PK of HBM9161 in MG Patients Myasthénie À vérifier Phase 2 COMPLETED Primary Objectives: To investigate the efficacy of HBM9161 in patients wit… À vérifier ClinicalTrials.gov 2026-07-10 00:13:41 Détail
Psychological Health and Adverse Childhood Experiences in Myasthenia… NCT07291713 · NCT07291713 Myasthénie Traitement symptomatique NA COMPLETED This study evaluated psychological health in patients with myasthenia grav… À vérifier ClinicalTrials.gov 2026-07-10 00:13:41 Détail
Quantification of Change in MG Disease Activity in Individuals With G… NCT07226830 · NCT07226830 Myasthénie Traitement symptomatique À vérifier NOT_YET_RECRUITING Evaluate the feasibility of using digital health technologies to monitor d… À vérifier ClinicalTrials.gov 2026-07-10 00:13:41 Détail
Behavioral Interventions for Controlling Oral Behaviors NCT07022795 · NCT07022795 Myopathies Traitement symptomatique NA RECRUITING Ecological momentary assessment (EMA) interventions via mobile devices can… À vérifier ClinicalTrials.gov 2026-07-10 00:13:40 Détail
Botulinum Toxin Type A for Injection NCT02280083 · A Study to Evaluate the Botulinum Toxin Type A for Injection(HengLi®) in Subject… Myopathies Ralentissement de la progression · Traitement symptomatique Phase 3 COMPLETED This is a multicenter, double-blind, randomized, placebo-controlled study… À vérifier ClinicalTrials.gov 2026-07-10 00:13:40 Détail
Capsaicin Topical Cream NCT07598994 · Topical Capsaicin Versus Diclofenac for Chronic Temporomandibular Joint-Related… Myopathies Traitement symptomatique NA COMPLETED The goal of this clinical trial is to compare the effectiveness and safety… À vérifier ClinicalTrials.gov 2026-07-10 00:13:40 Détail
Casimersen NCT03532542 · An Extension Study to Evaluate Casimersen or Golodirsen in Patients With Duchenn… Myopathies À vérifier Phase 3 TERMINATED The main objective of this study is to evaluate the safety and tolerabilit… À vérifier ClinicalTrials.gov 2026-07-10 00:13:40 Détail
Daratumumab Injection NCT04810754 · An Open Label Study to Evaluate Daratumumab in Participants With Moderate to Sev… Lupus À vérifier Phase 2 UNKNOWN This is a monocenter, open-label Phase II trial for refractory SLE patient… À vérifier ClinicalTrials.gov 2026-07-10 00:13:40 Détail
Desipramine NCT03726996 · Desipramine in Infantile Neuroaxonal Dystrophy (INAD). Myopathies Neuroprotection · Ralentissement de la progression · Traitement symptomatique Phase 4 TERMINATED This is a research study to find out if clinically prescribed desipramine… À vérifier ClinicalTrials.gov 2026-07-10 00:13:40 Détail
EEG NCT06449794 · Neuropsycatric Disorders Among Children With Systemic Lupus Erythematosus in Soh… Lupus Immunomodulation À vérifier UNKNOWN Systemic lupus erythematosus (SLE) is a chronic autoimmune disease involvi… À vérifier ClinicalTrials.gov 2026-07-10 00:13:40 Détail
Functional muscle transfer NCT04911972 · Functional Muscle Transfers in Lower Limb Sarcoma: 3D Gait Analysis and Environm… Myopathies À vérifier À vérifier COMPLETED The purpose of this study is to assess patient's function after functional… À vérifier ClinicalTrials.gov 2026-07-10 00:13:40 Détail
Gentamicin infusions twice a week for six months NCT00451074 · Six Month Study of Gentamicin in Duchenne Muscular Dystrophy With Stop Codons Myopathies À vérifier Phase 1 COMPLETED The purpose of this study is to determine the safety of giving intravenous… À vérifier ClinicalTrials.gov 2026-07-10 00:13:40 Détail
IvIg NCT00231439 · Post-Poliosyndrome Treated With Intravenous Immunoglobulin (IvIg) Myopathies Immunomodulation · Traitement symptomatique Phase 2 COMPLETED Inflammatory cytokines in the cerebrospinal fluid may contribute to the ne… À vérifier ClinicalTrials.gov 2026-07-10 00:13:40 Détail
KYV-101 NCT06152172 · CARTIMMUNE: Study of Patients With Autoimmune Diseases Receiving KYV-101 Lupus Immunomodulation · Thérapie cellulaire Phase 1 ACTIVE_NOT_RECRUITING The purpose of this study is to assess the safety, tolerability, and clini… À vérifier ClinicalTrials.gov 2026-07-10 00:13:40 Détail
Low Dose Mesenchymal Stem Cells (MSCs) NCT03171194 · Pilot Trial of Mesenchymal Stem Cells for Systemic Lupus Erythematosus Lupus Thérapie cellulaire Phase 1 COMPLETED The purpose of this study is to evaluate the safety of mesenchymal stromal… À vérifier ClinicalTrials.gov 2026-07-10 00:13:40 Détail
Oral Health, Saliva Viscosity and Composition in Oculo-Pharyngeal Mus… NCT07118280 · NCT07118280 Myopathies À vérifier À vérifier RECRUITING The goal of this observational study is to explore whether oral health and… À vérifier ClinicalTrials.gov 2026-07-10 00:13:40 Détail
Découverte scientifique

Recherches et trouvailles 21

Projets précliniques, publications émergentes et programmes de recherche suivis dans le pipeline.

Molécule / élément Maladie / population Objectif Phase / stade Statut / preuve Mécanisme / résumé Source Détail
4-octyl itaconate et dérivés Dérivés de l’itaconate — neuroinflammation Sclérose latérale amyotrophique Neuroprotection · Immunomodulation Découverte fondamentale Exploratoire Modulation immunométabolique de la microglie · NRF2 / inflammation microgl… Piste mécanistique visant à reprogrammer la réponse inflammatoire de la microglie. Le lien avec la SLA reste exploratoi… Revue scientifique 2024-07-01 Détail
Bibliographie

Publications 4595

Références bibliographiques de la base locale et accès à leur source originale.

Molécule / élément Maladie / population Objectif Phase / stade Statut / preuve Mécanisme / résumé Source Détail
Effects of testosterone-augmented multimodal exercise intervention in… Whole-body Electrical Muscle Stimulation Exercise · PMID 41988780 Myasthénie À vérifier Publication PubMed Voir la publication source Spinal cord injury (SCI) leads to profound muscle atrophy, aerobic deconditioning, and metabolic dysfunction. Exercise-… The Journal of clinical endocrinology and metabolism 2026-09-20 04:37:05 Source
Feasibility and acceptability of whole-body electromyostimulation in… Whole-body Electrical Muscle Stimulation Exercise · PMID 42464389 Myasthénie À vérifier Publication PubMed Voir la publication source Evidence on the effectiveness of electromyostimulation (EMS) has been reported in pulmonary rehabilitation, but the ben… Pilot and feasibility studies 2026-09-20 04:37:05 Source
Vestibular contributions adapt to the balance strategies adopted duri… Whole-body Electrical Muscle Stimulation Exercise · PMID 42616645 Myasthénie À vérifier Publication PubMed Voir la publication source Vestibular contributions during walking are not uniform, but vary with gait phase, muscle group, and balance demands. M… Journal of neurophysiology 2026-09-20 04:37:05 Source
Clinical efficacy of abdominal moxibustion at the Zhongji (CV3) in co… Yangyin Roujin Decoction · PMID 42015783 Myopathies Neuroprotection · Traitement symptomatique Publication PubMed Voir la publication source To investigate the clinical effect of abdominal moxibustion at the Zhongji (CV3) combined with Yiqi Tonglin Yangyin dec… Journal of traditional Chinese medicine = Chung i tsa… 2026-09-20 04:37:03 Source
Yiqi Huoxue Yangyin Decoction Ameliorates Diabetic Nephropathy by Tar… Yangyin Roujin Decoction · PMID 42713045 Myopathies À vérifier Publication PubMed Voir la publication source This study aimed to investigate the protective effects and underlying mechanisms of Yiqi Huoxue Yangyin Decoction (YHY)… Diabetes, metabolic syndrome and obesity : targets and… 2026-09-20 04:37:03 Source
Yiqi Huoxue Yangyin Decoction attenuates diabetic nephropathy in mice… Yangyin Roujin Decoction · PMID 42016924 Myopathies Thérapie génique Publication PubMed Voir la publication source Diabetic nephropathy (DN) is a major complication of diabetes with limited therapeutic options. Yiqi Huoxue Yangyin Dec… Frontiers in pharmacology 2026-09-20 04:37:03 Source
Barcoded oligonucleotide system (BOLT) for targeted organ delivery. Immunotherapy · PMID 42733790 Cancer À vérifier Publication PubMed Voir la publication source The therapeutic potential of oligonucleotides (oligos) is limited by insufficient delivery to extrahepatic tissues. In… Bioactive materials 2026-09-20 04:36:56 Source
Dual metabolic checkpoint blockade a 3D-Printed metalloplatform remod… Immunotherapy · PMID 42724565 Cancer Immunomodulation Publication PubMed Voir la publication source The immunosuppressive tumor microenvironment limits the efficacy of therapies that target metabolism. Here we show a st… Bioactive materials 2026-09-20 04:36:56 Source
Oligosaccharide adjuvant-deferred antigen endocytosis promotes cross-… Immunotherapy · PMID 42751513 Cancer Immunomodulation · Thérapie génique Publication PubMed Voir la publication source Antigen cross-presentation by dendritic cells (DCs) is essential for inducing cytotoxic immune responses, which are cru… Bioactive materials 2026-09-20 04:36:56 Source
Feasibility and safety of early discharge after robot-assisted uro-on… Digital care pathway for hypertension · PMID 42671715 Hypertension artérielle À vérifier Publication PubMed Voir la publication source Early discharge after robot-assisted uro-oncologic surgery remains limited by concerns regarding patient safety and the… Journal of robotic surgery 2026-09-20 04:36:49 Source
HomeSafe: Postpartum Hypertensive Care Enabled by Electronic Health R… Digital care pathway for hypertension · PMID 41707683 Hypertension artérielle À vérifier Publication PubMed Voir la publication source The objective is to present stepwise refinements to , an Epic-tethered, population-health-coordinated postpartum pathwa… American journal of perinatology 2026-09-20 04:36:49 Source
Nutraceutical and functional food: efficacy against metabolic disorde… Digital care pathway for hypertension · PMID 42603698 Hypertension artérielle Neuroprotection · Immunomodulation Publication PubMed Voir la publication source The growing global emphasis on health consciousness has significantly increased demand for traditional and complementar… Journal of advanced research 2026-09-20 04:36:49 Source
Community-engaged design of a virtual diabetes prevention program int… Asynchronous communication with nurse · PMID 42288862 Hypertension artérielle À vérifier Publication PubMed Voir la publication source The Diabetes Prevention Program (DPP) is an evidence-based approach to prevent Type 2 Diabetes (T2D), the leading cause… BMC health services research 2026-09-20 04:36:48 Source
Evolving Lung Cancer Navigator Practice Through Targeted Professional… Asynchronous communication with nurse · PMID 42463006 Cancer À vérifier Publication PubMed Voir la publication source Lung cancer remains the leading cause of cancer deaths worldwide, and it has persistent disparities in detection, treat… Chest 2026-09-20 04:36:48 Source
Mass casualty training for prehospital and emergency providers in Kig… Asynchronous communication with nurse · PMID 42751142 Hypertension artérielle À vérifier Publication PubMed Voir la publication source A mass casualty incident (MCI) occurs when the number of patients exceeds available healthcare resources, placing signi… African journal of emergency medicine : Revue africain… 2026-09-20 04:36:48 Source
Innovating a Teach-Back Model for Community Health Workers Led Health… Health Literacy Project · PMID 40194526 Épilepsie À vérifier Publication PubMed Voir la publication source From 2021 to 2023, the City of Albuquerque, the University of New Mexico (UNM) Office for Community Health, the UNM Hos… Health literacy research and practice 2026-09-20 04:36:34 Source
Carotid intima-media thickness may be an early biomarker for cardiova… Impact of Ketogenic Diets on Cardiovascular Health in Adults With Epilepsy · PMID 41026111 Épilepsie À vérifier Publication PubMed Voir la publication source To assess early signs of atherosclerosis following long-term treatment with the ketogenic diet therapy due to concerns… Epilepsia open 2026-09-20 04:36:33 Source
Impact of low-carbohydrate diet on health status: an umbrella review. Impact of Ketogenic Diets on Cardiovascular Health in Adults With Epilepsy · PMID 39385794 Cancer À vérifier Publication PubMed Voir la publication source The prevalence of diet-related non-communicable diseases has increased. A low-carbohydrate diet (LCDs) is one of the mo… Frontiers in nutrition 2026-09-20 04:36:33 Source
The effect of anti-seizure medications on lipid values in adults with… Impact of Ketogenic Diets on Cardiovascular Health in Adults With Epilepsy · PMID 37244221 Épilepsie À vérifier Publication PubMed Voir la publication source Certain anti-seizure medications (ASMs) adversely impact lipid values. Here, we explored the impact of ASMs on lipid va… Epilepsy & behavior : E&B 2026-09-20 04:36:33 Source
Possible role of locus coeruleus neuronal loss in age-related memory… The Role of the Locus Coeruleus in Age-related Distractibility · PMID 37694113 Maladie d’Alzheimer Immunomodulation Publication PubMed Voir la publication source Aging is associated with a decline in cognitive abilities, including memory and attention. It is generally accepted tha… Frontiers in neuroscience 2026-09-20 04:36:30 Source
Exploration — prudence

Pistes exploratoires 0

Rapprochements mécanistiques et hypothèses de recherche : ils ne constituent pas une preuve d’efficacité ni une recommandation thérapeutique.

Hypothèses non validéesÀ confirmer par des travaux précliniques, cliniques et une revue scientifique indépendante.
Molécule / élément Maladie / population Objectif Phase / stade Statut / preuve Mécanisme / résumé Source Détail
Aucune piste exploratoire ne correspond aux filtres.